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ANKS1B encoded AIDA-1 regulates social behaviors by controlling oligodendrocyte function.
Nat Commun. 2023 Dec 21;14(1):8499. doi: 10.1038/s41467-023-43438-1.
Nat Commun. 2023.
PMID: 38129387
Free PMC article.
Life-Limiting Peripheral Organ Dysfunction in Feline Sandhoff Disease Emerges after Effective CNS Gene Therapy.
Johnson AK, McCurdy VJ, Gray-Edwards HL, Maguire AS, Cochran JN, Gross AL, Skinner HE, Randle AN, Shirley JL, Brunson BL, Bradbury AM, Leroy SG, Hwang M, Rockwell HE, Cox NR, Baker HJ, Seyfried TN, Sena-Esteves M, Martin DR.
Johnson AK, et al. Among authors: maguire as.
Ann Neurol. 2023 Nov;94(5):969-986. doi: 10.1002/ana.26756. Epub 2023 Aug 16.
Ann Neurol. 2023.
PMID: 37526361
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White Matter Pathology as a Barrier to Gangliosidosis Gene Therapy.
Maguire AS, Martin DR.
Maguire AS, et al.
Front Cell Neurosci. 2021 Aug 12;15:682106. doi: 10.3389/fncel.2021.682106. eCollection 2021.
Front Cell Neurosci. 2021.
PMID: 34456684
Free PMC article.
Review.
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GM1 Gangliosidosis: Mechanisms and Management.
Rha AK, Maguire AS, Martin DR.
Rha AK, et al. Among authors: maguire as.
Appl Clin Genet. 2021 Apr 9;14:209-233. doi: 10.2147/TACG.S206076. eCollection 2021.
Appl Clin Genet. 2021.
PMID: 33859490
Free PMC article.
Review.
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Whole-slide image analysis outperforms micrograph acquisition for adipocyte size quantification.
Maguire AS, Woodie LN, Judd RL, Martin DR, Greene MW, Graff EC.
Maguire AS, et al.
Adipocyte. 2020 Dec;9(1):567-575. doi: 10.1080/21623945.2020.1823139.
Adipocyte. 2020.
PMID: 32954932
Free PMC article.
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7T MRI Predicts Amelioration of Neurodegeneration in the Brain after AAV Gene Therapy.
Gray-Edwards HL, Maguire AS, Salibi N, Ellis LE, Voss TL, Diffie EB, Koehler J, Randle AN, Taylor AR, Brunson BL, Denney TS, Beyers RJ, Gentry AS, Gross AL, Batista AR, Sena-Esteves M, Martin DR.
Gray-Edwards HL, et al. Among authors: maguire as.
Mol Ther Methods Clin Dev. 2019 Dec 24;17:258-270. doi: 10.1016/j.omtm.2019.11.023. eCollection 2020 Jun 12.
Mol Ther Methods Clin Dev. 2019.
PMID: 31970203
Free PMC article.
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A Safe and Reliable Technique for CNS Delivery of AAV Vectors in the Cisterna Magna.
Taghian T, Marosfoi MG, Puri AS, Cataltepe OI, King RM, Diffie EB, Maguire AS, Martin DR, Fernau D, Batista AR, Kuchel T, Christou C, Perumal R, Chandra S, Gamlin PD, Bertrand SG, Flotte TR, McKenna-Yasek D, Tai PWL, Aronin N, Gounis MJ, Sena-Esteves M, Gray-Edwards HL.
Taghian T, et al. Among authors: maguire as.
Mol Ther. 2020 Feb 5;28(2):411-421. doi: 10.1016/j.ymthe.2019.11.012. Epub 2019 Nov 16.
Mol Ther. 2020.
PMID: 31813800
Free PMC article.
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Novel Biomarkers of Human GM1 Gangliosidosis Reflect the Clinical Efficacy of Gene Therapy in a Feline Model.
Gray-Edwards HL, Regier DS, Shirley JL, Randle AN, Salibi N, Thomas SE, Latour YL, Johnston J, Golas G, Maguire AS, Taylor AR, Sorjonen DC, McCurdy VJ, Christopherson PW, Bradbury AM, Beyers RJ, Johnson AK, Brunson BL, Cox NR, Baker HJ, Denney TS, Sena-Esteves M, Tifft CJ, Martin DR.
Gray-Edwards HL, et al. Among authors: maguire as.
Mol Ther. 2017 Apr 5;25(4):892-903. doi: 10.1016/j.ymthe.2017.01.009. Epub 2017 Feb 22.
Mol Ther. 2017.
PMID: 28236574
Free PMC article.
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